Necrotizing Enterocolitis Following Onasemnogene Abeparvovec for Spinal Muscular Atrophy: A Case Series

Onasemnogene abeparvovec treats spinal muscular atrophy (SMA) by delivering a functional SMN1 gene. Necrotizing enterocolitis (NEC) typically occurs in preterm infants. We report two term infants diagnosed with SMA who presented with NEC after onasemnogene abeparvovec infusion. We discuss potential etiologies and propose monitoring for NEC after onasemnogene abeparvovec therapy.

source https://www.jpeds.com/article/S0022-3476(23)00341-4/fulltext?rss=yes

Comments

Post a Comment

Popular posts from this blog

Out Of The Old Black Bag

Image
  OUT OF THE OLD BLACK BAG   Remediating the Past: Reactive Attachment Disorder Part 2: Society’s Emotional Orphans By  Anthony Kovatch, M.D.   Musical Accompaniment : “The Story In Your Eyes” by The Moody Blues.   *   *   *   *   *   *   *   *   *   *   “ The most important people in a child’s life are that child’s parents and teachers.   That means parents and teachers are the most important people in the world.” Mister Rogers     Every child wants to live in Mister Rogers’ neighborhood — and every adult, too!   *   *   *   *   *   *   *   *   *   *   The DSM-V recognizes two distinct forms of attachment disorder: Reactive Attachment Disorder (RAD) and Disinhibited Social Engagement Disorder (DSED). The first involves the inability to attach to a preferred caregiver, and the second involves indiscriminate sociabili...
Read more

Medical School in The Fall

Fall in St. Kitts sets a picturesque backdrop for our student’s medical journey. With the vibrant colors of nature & the warmth of the Caribbean sun, the UMHS campus becomes an oasis for academic learning & development as a student. The Fall semester brings a new sense of focus & determination as students dive into their studies, partake in campus club activities, & explore the island of St. Kitts. Interested in becoming a UMHS student? View our website @ https://www.umhs-sk.org/ #fall2023 #medicalschoollife #campustour #medicalcampus #umhsstkitts from University of Medicine and Health Sciences https://www.youtube.com/watch?v=Waj_qu0I7xk via UMHS YouTube Channel
Read more